ProQR Announces Positive Top-Line Results from a Phase 1b

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Patient-Centric Approach menu item, submenu; Global Compliance Program menu item, submenu 2017-05-01 · Next in ProQR’s ophthalmology pipeline are two programs each targeting specific mutations that result in Usher syndrome. QRX-411 and QRX-421 are candidate molecules that will be presented in two 2019-05-17 · Wings Therapeutics has assumed control of ProQR’s pipeline dedicated to DEB and will take over the ongoing Phase 1/2 WINGS trial (NCT03605069) testing QR-313 for patients with recessive DEB due to mutations in exon 73 of the COL7A1 gene. Key program features and updates: ProQR to host an R&D day in New York today, June 15, from 8:00am to 1:00pm Eastern Standard Time. The live webcast can be accessed at | April 23, 2021 2021-04-20 · LEIDEN, Netherlands & CAMBRIDGE, Mass., April 20, 2021 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (Nasdaq: PRQR) (the “Company”), a company dedicated to changing lives through the creation of transformative RNA therapies for inherited retinal diseases (IRDs), today announced the Annual General Meeting of Shareholders will take place on Wednesday, May 19, 2021 at 16:00 CET (10:00am EDT Despite this, ProQR can still be a very interesting candidate to add to your watchlist. Hence, it is necessary to have a closer look at the company’s current situation, including its pipeline Company Overview. ProQR has a U.S. campus in Cambridge, Mass., but is headquartered out of The Netherlands.

Proqr pipeline

The company's main product candidates are QR-010, QR-110, and QR-313. Its product pipeline We are ProQR. About us; Vision 2023; Leadership; Careers; Contact; Science & Pipeline. Research and development pipeline; Clinical Trials. QR-1123 Aurora phase 1/2 study for adRP; Sepofarsen ILLUMINATE phase 2/3 study for LCA10; QR-421a STELLAR phase 1/2 study for Usher syndrome; Sepofarsen INSIGHT – phase 1b/2 study for LCA10; Sepofarsen Proven leader with deep worldwide ophthalmology experience, including multiple approvals globallyLEIDEN, Netherlands & CAMBRIDGE, Mass., Oct. 05, 2020 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V LEIDEN, Netherlands & CAMBRIDGE, Mass., Oct. 05, 2020 (GLOBE NEWSWIRE) -- ProQR Based on our unique proprietary RNA repair platform technologies we are growing our pipeline with ProQR expanded its platform and pipeline with QR-110 for the treatment of Leber's Congenital Amaurosis (LCA), the leading genetic cause of blindness in childhood.

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It discovers and develops Its product pipeline includes QRX-704, QRX-504, QRX-421, QRX- 323 etc. 03, 2019 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (Nasdaq:PRQR) will ProQR and external speakers on the progress of the ophthalmology pipeline, The company's growing pipeline is based on its proprietary technology platform of RNA technologies. • Its lead program is eluforsen (formerly QR-010), which is 25 Mar 2021 The Cystic Fibrosis (Respiratory) pipeline guide also reviews of key Progenra Inc; ProQR Therapeutics NV; Protalix BioTherapeutics Inc The company was founded in 2019 by EB Research partnership and ProQR Therapeutics to continue development of a pipeline of potential RNA therapies for Its product pipeline inlcude Sepofarsen , QR-421a, QR-1123, and QR-504a.

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“On the basis of this performance, we begin 2021 in a strong position to deliver on a number of important catalysts across our pipeline, including the next interim ProQR Therapeutics is a clinical-stage biotech company with offices in Leiden, the Netherlands and Cambridge, Massachusetts, US. ProQR is focused on the ophthalmology candidates in our pipeline, as we believe that RNA oligonucleotides hold great promise for the treatment of a variety of genetic eye diseases.”. Science & Pipeline SubmenuScience & Pipeline. Pipeline · Sepofarsen (CEP290 LCA10) · QR-421a (USH2A RP) · QR-1123 (RHO RP) · Presentations & QR-421a is part of ProQR's growing ophthalmology pipeline which also includes lead candidate, QR-110 for Leber's congenital amaurosis 10 currently in 14 Jul 2020 “Pontifax is pleased to enter into this strategic financing partnership with ProQR as it continues to advance its pipeline of RNA therapies for Based on our unique proprietary RNA repair platform technologies we are growing our pipeline with patients and loved ones in mind. Learn more about ProQR ProQR expanded its platform and pipeline with QR-110 for the treatment of Leber's Congenital Amaurosis (LCA), the leading genetic cause of blindness in 6 Aug 2020 06, 2020 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (Nasdaq: our pipeline,” said Daniel A. de Boer, Chief Executive Officer of ProQR. At ProQR we develop antisense oligonucleotides, or RNA therapies, to treat genetic diseases that are rare. We have made significant progress in advancing our ProQR was founded in 2012 by CEO Daniel de Boer and co-founders Henri Termeer, Dinko Valerio and Gerard Platenburg.

In the trial, QR-421a demonstrated benefit on multiple measures of vision that moved in concordance, including visual acuity, visual fields, and optical coherence tomography (OCT We are ProQR Therapeutics, a biotech company based in Leiden, the Netherlands and Cambridge, MA. We develop RNA therapies for inherited retinal diseases, with a high need for new medicines. The vast m. Leiden. 3 Tracks. 3 Followers.
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LEIDEN, Netherlands and CAMBRIDGE, Mass., March 30, 2021 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (NASDAQ: PRQR), a company dedicated to changing lives through the creation of transformative RNA therapies for inherited retinal diseases (IRDs), today announced the pricing of its previously announced underwritten public offering of 13,846,154 ordinary shares at a price to the public of $6.50 per share. The therapies in the ProQR pipeline utilize an RNA oligonucleotide technology platform to repair genetic defects, targeting significant parts of the mutations that are known causes of inherited Wings Therapeutics has assumed control of ProQR’s pipeline dedicated to DEB and will take over the ongoing Phase 1/2 WINGS trial (NCT03605069) testing QR-313 for patients with recessive DEB due to mutations in exon 73 of the COL7A1 gene. ProQR Therapeutics NV is a biopharmaceutical company, which engages in the discovery and development of RNA therapies for the treatment of severe genetic rare diseases such as Leber congenital amaurosis 10, Usher syndrome and retinitis pigmentosa. Its product pipeline include Sepofarsen, QR-421a, QR-1123, and QR-504a. LEIDEN, Netherlands & CAMBRIDGE, Apr 23, 2021 (GLOBE NEWSWIRE via COMTEX) -- LEIDEN, Netherlands & CAMBRIDGE, Mass., April 23, 2021 (GLOBE NEWSWIRE) -- The therapies in the ProQR pipeline utilize an RNA oligonucleotide technology platform to repair genetic defects, targeting significant parts of the mutations that are known causes of inherited ProQR Therapeutics is dedicated to changing lives through the creation of transformative RNA therapies for the treatment of severe genetic rare diseases such as Leber congenital amaurosis 10 ProQR was founded in 2012 by CEO Daniel de Boer and co-founders Henri Termeer, Dinko Valerio and Gerard Platenburg. The company’s current pipeline includes potential treatments for rare genetic diseases including Leber's congenital amaurosis, (LCA10) dystrophic epidermolysis bullosa and Usher syndrome. ProQR R&D day Highlights Progress on Pipeline and Introduces Axiomer®, a novel proprietary RNA Technology ProQR to host an R&D day in New York today, June 15, from 8:00am to 1:00pm Eastern Standard Time.

The product candidates in ProQR’s pipeline target diseases with a well-understood genetic cause where rational drug design can be applied to yield RNA molecules with therapeutic potential. 2021-03-24 · “We are pleased to see QR-421a advancing to pivotal testing and proud to support the work of ProQR as they advance their pipeline of RNA therapies to potentially help children, adults, and families who are affected by blindness caused by USH2A mutations and other rare inherited retinal diseases.” Phase 1/2 Stellar trial of QR-421a ProQR Therapeutics N.V.: Investor Contact: Sarah Kiely ProQR Therapeutics N.V. T: +1 617 599 6228 skiely@proqr.com or Hans Vitzthum LifeSci Advisors T: +1 617 430 7578 hans@lifesciadvisors.com 2020-03-31 · ProQR Therapeutics N.V. Investor Contact: Sarah Kiely ProQR Therapeutics N.V. T: +1 617 599 6228 skiely@proqr.com or Hans Vitzthum LifeSci Advisors T: +1 617 430 7578 hans@lifesciadvisors.com QR-313 is the short term catalyst amongst many that ProQR has in their pipeline. The company is expected to present Phase I/II interim data in the first quarter of 2019. With March newly here, the company is approaching the timeline that they set out. Summary. Ophthalmic RNA therapy concern ProQR Therapeutics N.V. (PRQR) has seen its share price more than half since its 2014 IPO. Promising Phase 1/2 data from its lead candidate (sepofarsen) has Key program features and updates: ProQR to host an R&D day in New York today, June 15, from 8:00am to 1:00pm Eastern Standard Time. The live webcast can be accessed at | February 28, 2021 2016-03-01 · ProQR to Highlight a Growing Pipeline During a Research & Development Day and Present at the Barclays Global Healthcare Conference.
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Visit website. ProQR our strategy to create a well-diversified pipeline of medicine candidates in several therapeutic areas. In this report, we tell you about how ProQR progressed in Based on its unique proprietary RNA repair platform technologies, ProQR Therapeutics is growing its pipeline with patients and loved ones in mind. Apr 2, 2021 Based on our unique proprietary RNA repair platform technologies we are growing our pipeline with patients and loved ones in mind.Learn more ProQR Therapeutics is developing RNA-based therapeutics for the treatment of genetic QRX 203 is undergoing early research development (ProQR pipeline, ProQR was founded in 2012 by CEO Daniel de Boer and co-founders Henri Termeer, Dinko Valerio and Gerard Platenburg. The company's current pipeline Feb 26, 2021 “On the basis of this performance, we begin 2021 in a strong position to deliver on a number of important catalysts across our pipeline, including Mar 24, 2021 pipeline candidates, QR-421a.

Pipeline. Sepofarsen (CEP290 LCA10) QR-421a (USH2A RP) QR-1123 (RHO RP) Presentations & Publications; RNA therapy.
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We aim to make a difference for these patients as we work to advance our pipeline of programs to treat inherited retinal diseases.” About QR-421a. QR- 421a is a Science & Pipeline SubmenuScience & Pipeline. Pipeline · Sepofarsen (CEP290 LCA10) · QR-421a (USH2A RP) · QR-1123 (RHO RP) · Presentations & Mar 24, 2021 “We are pleased to see QR-421a advancing to pivotal testing and proud to support the work of ProQR as they advance their pipeline of RNA ProQR's ophthalmology pipeline includes the following: QRX-421 for Usher syndrome type 2 due to exon 13 mutations in the USH2A gene, for which a clinical At ProQR we develop antisense oligonucleotides, or RNA therapies, to treat genetic diseases that are rare. We have made significant progress in advancing our Based on their unique proprietary RNA repair platform technologies they are growing their pipeline with patients and loved ones in mind. Visit website. ProQR our strategy to create a well-diversified pipeline of medicine candidates in several therapeutic areas. In this report, we tell you about how ProQR progressed in Based on its unique proprietary RNA repair platform technologies, ProQR Therapeutics is growing its pipeline with patients and loved ones in mind.

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ProQR Doses First Patient in Phase 1/2 STELLAR Trial of QR

LEIDEN, Netherlands, Nov. 30, 2015 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (Nasdaq:PRQR), a company dedicated to changing lives through the creation of transformative RNA medicines for the treatment of severe orphan diseases such as cystic fibrosis (CF) and Leber's congenital amaurosis (LCA), today presents an update on the innovation pipeline and announces an R&D day for investors. 2021-03-25 · ProQR Therapeutics shares reached a new 52-week high after the company reported highly positive results from its Phase 1/2 Stellar trial of QR-421a in adults with Usher syndrome and non-syndromic retinitis pigmentosa (nsRP) due to USH2A exon 13 mutations. ProQR plans to independently advance its pipeline of RNA medicines to establish a multi-product, platform company in IRD. By 2023, the company expects its pipeline to have at least two commercial products, and at least three late-stage and seven early-stage programs in development.